2025 Global Gene Therapy Training

Thank you for your interest in this course! Applications for 2025 are now closed.

What to Expect

Watch a preview of a course below.

Course Structure - NEW FORMAT for 2025

This course is for academic faculty teaching at accredited universities or medical schools in sub-Saharan Africa. The course aims to train faculty with the necessary knowledge and skills to implement gene therapy education into their university and medical school curricula.  

This program features a flexible, on-demand format with short, easy-to-follow videos released at the start of the course, along with a suggested learning path to guide participants. Weekly live “office hours” sessions with course experts will provide opportunities for real-time Q&A and community engagement on specific topics. To earn a certificate, participants must complete a pre-test, post-test, and four weekly course assessments, achieving a cumulative average score of at least 70%—with retakes allowed.  

Course Topics + Office Hours Schedule

• Week 1 courses + Office Hours  

  • Courses 1-3 published: Monday, June 2 

    • Genetics of Human Disorders 

    • Gene Therapy Overview, Part 1 

    • Gene Therapy Overview, Part 2 

  • Office Hours: Tuesday, June, 10, 2025 from 8-9 am CDT/ 4-5 pm EAT (tentative)  

• Week 2 courses + Office Hours  

  • Courses 4-5 published: Monday June 9 

    • Methods for Correcting Genetic Disease 

    • Use of Gene Therapy in Cancer Treatment  

  • Office Hours: Tuesday, June 17, 2025 from 8-9 am CDT/ 4-5 pm EAT (tentative)  

• Week 3 courses + Office Hours  

  • Courses 6-7 published: Monday, June 16 

    • Current Status of Clinical Gene Therapy 

    • Ethics Issues, Regulatory Issues, and the Role of Patient Advocacy Groups and International Partnerships in Implementing Gene Therapies 

  • Office Hours: Tuesday, June 24, 2025 from 8-9 am CDT/ 4-5 pm EAT (tentative) 

• Week 4 courses + Office Hours  

  • Course 8 published: Monday, June 23 

    • Planning a Step-Down Training 

    • Gene Therapy in Africa  

  • Office Hours: Tuesday, July 1, 2025 from 8-9 am CDT/ 4-5 pm EAT (tentative) 

Objectives

Participants completing the course will learn: 

1. Methods used in genetic modification of human tissues    

2. Major disease targets for clinical gene therapies   

3. Ethical and regulatory challenges to gene therapies   

4. Limitation and opportunities for equitable access to gene therapy  

Outcomes 

At the conclusion of the course the participant will be able to: 

1. Explain the methods used in clinical gene therapy    

2. Summarize the status of gene therapy clinical trials   

3. Critique the ethical and regulatory issues regarding genetic modification of human tissues   

4. Create educational materials to educate trainees on the current status of clinical gene therapy 

Requirements 

Participants must complete all pre- and post-tests, view all eight on-demand modules, and complete all four assessments with a score of 70% or higher. Meeting these requirements will result in a certificate from MUHAS and ASGCT. 

Apply for the Global Gene Therapy Training Course