2024 Archive

Read and Download 2024 Reports

Learn about new approvals and the state of the field for each quarter of 2024.

Q1 2024

The field earned the approval of three new therapies—a CAR-T therapy for myeloma in China, an AAV gene therapy for hemophilia B in Canada, and an autologous cell therapy for melanoma in the United States.

Q2 2024

In Q2, two new RNA therapies were approved in the US; Rytelo was approved for myelodysplastic syndrome and mRESVIA, an mRNA vaccine, was approved for respiratory syncytial virus (RSV) prophylaxis.

Q3 2024

While we saw only one new approval (Tecelra for synovial sarcoma), there are dynamic shifts deeper in the pipeline. The field is steadily diversifying; 51% of newly initiated gene therapy trials are now for non-oncology indications, up from just 39% year-over-year.

2025

Class Considerations on Immunogenicity for AAV GT Products

January 22-23, 2025 | Virtual

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