Learn About Gene Therapy for Huntington’s Disease

The American Society of Gene & Cell Therapy (ASGCT) released its latest resource profiling disease-specific treatment efforts, this time focusing on developing gene therapies for Huntington’s disease.

Watch ASGCT's Gene Therapy for Huntington's Disease Video

The resources on Huntington’s disease are now available on ASGCT.org. Huntington’s disease is a genetic disorder caused by a breakdown of nerve cells in the brain. The disease affects an individual’s ability to move, their mood, and how they think. There’s currently no cure for Huntington’s disease, but there are types of gene therapy approaches that may offer hope for managing or slowing symptoms. Learn more about gene therapies currently being researched to treat Huntington’s disease here.

The information on Huntington’s disease is part of the launch of a second round of material in ASGCT’s Patient Education program. ASGCT will release brand new resources weekly through the end of November on the Patient Education portal. Designed by ASGCT committee volunteers in coordination with patient advocacy groups, the patient-centered portal aims to educate and inform patients, families, and the public on the status and promise of gene and cell therapies.

The full schedule for ASGCT’s new Patient Education resources to be released during the remainder of 2019, excepting one-week breaks for the ASGCT Policy Summit and Thanksgiving, is as follows:

• Muscular dystrophy—October 24
• MPS (Mucopolysaccharidosis)—October 29
• Hemophilia— November 12
• Pompe—November 19
• CAR T Basics—December 3

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