Gene Editing

Find presenter-approved materials from the Gene Editing ASGCT Pre-Meeting Workshop

The Gene Editing workshop provides an overview of current gene editing technologies and approaches, emerging uses and applications, with sessions highlighting junior investigators and clinical gene editing programs.

2019 Workshop Materials

Precision Genetic Medicines Through Base Editing

Giuseppe Ciaramella, Ph.D.—Beam Therapeutics

Efficient in Vivo RNP-based Gene Editing in the Sensory Organ Inner Ear Using Bioreducible Lipid Nanoparticles (bLNPs)

Zheng-Yi Chen, D.Phil.—Mass Eye & Ear Infirmary/Harvard Medical School

Intro: ASGCT 2019 Annual Meeting Pre-Meeting Gene Editing Workshop

Morgan L. Maeder, Ph.D.—Third Rock Ventures NewCo

Advanced Genetic Engineering of Hematopoiesis for the Treatment of Inherited Diseases

Pietro Genovese, Ph.D.—San Raffaele Scientific Institute Telethon Institute for Gene Therapy

Enhancing Genome Editing with Engineered CRISPR Enzymes

Benjamin Kleinstiver, Ph.D.—Massachusetts General Hospital

NIH Somatic Cell Genome Editing Consortium (SCGE)

Betty Poon, Ph.D.—National Institute of Allergy and Infectious Diseases (NIAID)

Guide Identification for CRISPR-Cas9 Engineering of Allogeneic T Cell Therapies

Shawdee Eshghi, PhD

Genome Editing for Pediatric Diseases

Fred Chereau